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Duchenne Muscular Dystrophy Clinic

UR Medicine / Neurology / Our Divisions / Neuromuscular Disease Center / Multidisciplinary Clinics / Duchenne Muscular Dystrophy Clinic / Research and Clinical Trials
 

Research and Clinical Trials

If you are interested in receiving information about clinical trials available for Duchenne Muscular Dystrophy please email Dr. Ciafaloni.

Current Clinical Trials

FOR-DMD

 

  1. FOR-DMD: Double-blind randomized trial to optimize steroid regimen in Duchenne MD (1 R01 NS061799-01A2)
  2. An Open-Label, Multi-Center Study to Evaluate the Safety and Tolerability of Eteplirsen in Patients with Advanced Stage Duchenne Muscular Dystrophy (Sarepta)
  3. An Open-Label, Multi-Center, 48-Week Study with a Concurrent Untreated Control Arm to Evaluate the Efficacy and Safety of Eteplirsen in Duchenne Muscular Dystrophy (Sarepta)
  4. A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy (Marathon Pharmaceuticals, LLC)
  5. An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability of Deflazacort in Duchenne Muscular Dystrophy (Marathon Pharmaceuticals, LLC)